Question to the Department of Health and Social Care:

To ask the Secretary of State for Health and Social Care, what steps his Department is taking to improve access to treatments to manage Fanconi Anaemia.

Working under the UK Rare Diseases Framework, the Government is committed to improving the lives of those living with rare diseases, such as Fanconi Anaemia. The UK Rare Diseases Framework sets out four priorities collaboratively developed with the rare disease community. The fourth priority of the framework is improved access to specialist care, treatment, and drugs. Action under this priority has included reviewing the medicines access pathways, namely the Early Access to Medicines Scheme, the Innovative Licensing Pathway, and the Innovative Medicines Fund, for their suitability for rare disease therapies and reforming clinical trial regulations. Information on Fanconi Anaemia is included on the NHS England GeNotes page, supporting healthcare professionals with easy access to information on the diagnosis and treatment of this condition.