Rare Diseases: Genetic Engineering

(asked on 19th July 2021) - View Source

Question to the Department of Health and Social Care:

To ask the Secretary of State for Health and Social Care, with reference to the UK Rare Diseases Framework, whether he has had discussions with NICE on concerns arising from the first gene therapy for a rare disease to go through NICE's appraisal process having been rejected.


Answered by
Jo Churchill Portrait
Jo Churchill
Minister of State (Department for Work and Pensions)
This question was answered on 27th July 2021

We have had no specific discussions. The National Institute for Health and Care Excellence (NICE) is responsible for developing its recommendations independently and in accordance with its methods and processes. NICE has recommended a number of cell and gene therapies through its technology appraisal programme and these treatments are now available to National Health Service patients in line with NICE’s recommendations.

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