Rare Diseases: Drugs
(asked on 4th January 2019) - View Source
Question to the Department of Health and Social Care:
To ask the Secretary of State for Health and Social Care, what proportion of the rare disease medicines that do not meet the Highly Specialised Technology Criteria have been approved for access by NICE.
This question was answered on 14th January 2019
The National Institute for Health and Care Excellence has advised that it has published 48 technology appraisals of orphan medicines for rare diseases, of which it has recommended 75% for some or all of the eligible patient population.